Chapter 38  ·  Module 2
Antiprotozoal Agents
Nitroimidazoles, trypanosomiasis, Chagas disease, leishmaniasis, and toxoplasmosis
Abbreviations: NECT = nifurtimox-eflornithine combination therapy  ·  DHFR = dihydrofolate reductase  ·  DHPS = dihydropteroate synthase  ·  HIV = human immunodeficiency virus  ·  PCR = polymerase chain reaction  ·  HAT = human African trypanosomiasis
Metronidazole — Nitroimidazole Class
Mechanism
Anaerobic Reductive Activation
  • Prodrug: reduced by ferredoxin in anaerobic organisms
  • Reactive nitroso radical → DNA strand breaks
  • Mammalian cells lack ferredoxin → selective toxicity
  • Tinidazole: same mechanism, longer half-life, single-dose options
Key Clinical Points
Spectrum and Interactions
  • Protozoa: Giardia, Entamoeba, Trichomonas
  • Bacteria: Bacteroides, Clostridium, anaerobes
  • Amebic liver abscess: add luminal agent (diloxanide or iodoquinol)
  • Alcohol: disulfiram-like reaction (acetaldehyde accumulation)
  • Warfarin: potentiated via CYP2C9 inhibition
Human African Trypanosomiasis (HAT) — Stage-Dependent Treatment
Treatment by Stage and Subspecies
Stage T. b. gambiense T. b. rhodesiense Key Mechanism
Stage 1 (blood) Pentamidine Suramin No blood-brain barrier penetration needed
Stage 2 (CNS) NECT (nifurtimox + eflornithine) Melarsoprol Blood-brain barrier penetration required
Eflornithine Selectivity

Irreversible ornithine decarboxylase inhibitor → blocks polyamine synthesis. T. b. gambiense has slower ornithine decarboxylase turnover than T. b. rhodesiense → sustained inhibition in gambiense only. Melarsoprol: arsenic binds trypanothione → kills both subspecies in stage 2 but causes post-treatment reactive encephalopathy.

Chagas Disease and the Trypanothione System
Chagas Disease
Benznidazole / Nifurtimox
  • Benznidazole: nitroimidazole; reductive activation by T. cruzi nitroreductases → DNA/protein damage
  • Nifurtimox: nitrofuran; generates reactive oxygen species → overwhelms trypanothione
  • Acute phase and congenital disease: high cure rates
  • Chronic cardiomyopathy: reduces PCR positivity; cardiac benefit unproven (BENEFIT trial)
  • Both agents: teratogenic — contraindicated in pregnancy
Shared Vulnerability
Trypanothione System
  • Trypanosoma and Leishmania use trypanothione (not glutathione) as primary antioxidant
  • Absent in mammalian cells → selective drug target
  • Melarsoprol: arsenic binds trypanothione directly
  • Nifurtimox: reactive oxygen species overwhelm trypanothione
  • Antimonials (Sb III): inhibit trypanothione reductase
  • Eflornithine: depletes polyamine precursors for trypanothione synthesis
Leishmaniasis — Drug Selection by Form and Region
First-Line Visceral
Liposomal Amphotericin B
  • Binds Leishmania membrane sterols → lethal ion flux
  • Liposomal: targets reticuloendothelial system where amastigotes live
  • Reduced nephrotoxicity vs conventional form
  • HIV coinfection: indefinite secondary prophylaxis required
First Oral Agent
Miltefosine
  • Alkylphosphocholine → disrupts Leishmania membrane phospholipids
  • First-line in South Asia (antimonial resistance prevalent)
  • Teratogenic — contraception mandatory during and after treatment
  • Long half-life: resistance selection risk
Legacy Agents
Antimonials / Pentamidine
  • Antimonials (Sb V → Sb III): inhibit trypanothione reductase; resistance high in South Asia
  • Pentamidine: disrupts kinetoplast DNA; severe hypoglycemia risk
  • Antimonials still active in East Africa and parts of South America
Toxoplasmosis — Sequential Folate Blockade
Standard Treatment
Pyrimethamine + Sulfadiazine
  • Sulfadiazine: inhibits DHPS (early folate synthesis step)
  • Pyrimethamine: inhibits DHFR (downstream folate step)
  • Sequential double blockade → synergistic antiparasitic effect
  • Folinic acid (leucovorin) mandatory: bypasses DHFR block in human cells
  • Folic acid does NOT substitute — cannot bypass DHFR block
Prophylaxis
Trimethoprim-Sulfamethoxazole
  • Preferred primary prophylaxis in HIV with advanced immunosuppression
  • Also covers Pneumocystis jirovecii pneumonia simultaneously
  • Discontinue after sustained immune reconstitution on antiretroviral therapy
  • Spiramycin: reduces vertical transmission in pregnancy (does not treat established fetal infection)