Methylxanthines, Leukotriene Modifiers, and Mast Cell Stabilizers
Theophylline pharmacokinetics, leukotriene pathway targets, and aspirin-exacerbated respiratory disease
Theophylline: Mechanism and Toxicity
Mechanism
Dual Action
  • PDE3/PDE4 inhibition → cyclic AMP ↑ → bronchodilation
  • Adenosine A1/A2B antagonism → bronchodilation + mast cell inhibition
  • Therapeutic window: 10–20 mcg/mL
  • Non-linear kinetics — small dose Δ = large level Δ
Toxicity
Organ System Effects
  • GI: nausea, vomiting (earliest sign)
  • CNS: seizures (refractory to anticonvulsants)
  • Cardiac: tachycardia, arrhythmias
  • Smoking cessation → levels rise (CYP1A2 loss)
Leukotriene Pathway: Drug Targets
Zileuton Montelukast Zafirlukast Cromolyn
Target5-LipoxygenaseCysLT1 receptorCysLT1 receptorMast cell
Dosing4× dailyOnce dailyTwice daily4× daily
Key concernCYP1A2 inhibitor; hepatotoxicityNeuropsychiatric black boxDrug interactionsLess effective than ICS
Use in AERDYesYes — preferredYesNo
Aspirin-Exacerbated Respiratory Disease
Triad
Clinical Presentation
  • Asthma
  • Nasal polyps / chronic rhinosinusitis
  • Aspirin / NSAID hypersensitivity
  • Reaction within 30–180 min of ingestion
Mechanism and Management
COX-1 Inhibition → LT Surge
  • COX-1 blocked → PGE2 falls → 5-LOX unopposed
  • Cysteinyl leukotriene surge → bronchoconstriction
  • Safe: acetaminophen <1g; celecoxib
  • Treat with LTRAs; avoid NSAIDs